Cristina Liberati

Cristina Liberati

POSTDOC ASO

Department: MD-CHILD HEALTH RES INSTITUTE
Business Phone: (352) 294-8706
Business Email: c.liberati@peds.ufl.edu

Publications

2019
Clinical Muscle Gene Therapy (chapter 44) and Preclinical Gene Therapy Studies for Metabolic Myopathy (chapter 33)
Muscle Gene Therapy (by Dongsheng Duan & Jerry R. Mendell). 2nd ed:759-774
2017
Safety of Intradiaphragmatic Delivery of Adeno-Associated Virus-Mediated Alpha-Glucosidase (rAAV1-CMV-hGAA) Gene Therapy in Children Affected by Pompe Disease.
Human gene therapy. Clinical development. 28(4):208-218 [DOI] 10.1089/humc.2017.146. [PMID] 29160099.

Contact Details

Phones:
Business:
(352) 294-8706
Emails: