Helpful Links

 

Muscular Dystrophy Association Parent Project Muscular Dystrophy Know Your Duchenne
 Barth Syndrome Fondation  National Organization for Rare Disorders  Genetics Home Reference
 MTM-CNM Family Connection  Joshua Frase Foundation
 Friedrich's Ataxia Research Alliance  Myotonic Dystrophy Foundation  American Heart Association
 Cardiomyopathy UK  Cure Duchenne  Camp Boggy Creek
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 Study Sponsor Links

Solid Biosciences  

Sarepta Therapeutics

 

 

Audentes Therapeutics

 

Genzyme Amicus Therapeutics BioMarin
 

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Sanofi Roche  

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