Pompe Disease Category Amicus Therapeutics Announces First Patient Dosed in Phase 3 PROPEL in Pompe Published: Dec 20th, 2018 Accelerated Approval Denied & Study Underway for Pompe Treatment Published: Sep 10th, 2018 UF & MDA Host 2018 Pompe Disease Patient Meeting Published: Jul 30th, 2018 Developing Personalized CRISPR-Cas9 Genome Editing Therapy for Pompe Disease Published: Jul 18th, 2018 Amicus Announces Regulatory/Clinical Updates for AT-GAA in Pompe Published: Jul 6th, 2018 Gene therapy for pulmonary dysfunction in Pompe Published: Feb 19th, 2018 Valerion Initiates VAL-1221 Dosing in Patients with Pompe Published: Jul 11th, 2017 The backstory behind the Pompe patient Trump highlighted to Congress Published: Mar 2nd, 2017 The 2017 Rare Disease Day video! Published: Jan 30th, 2017 UF researchers use gene therapy to treat pulmonary dysfunction in Pompe Published: Sep 15th, 2016 Page 1 of 3123