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Amicus Therapeutics

Amicus Therapeutics Announces First Patient Dosed in Phase 3 PROPEL in Pompe

Published: Dec 20th, 2018

Lab

Accelerated Approval Denied & Study Underway for Pompe Treatment

Published: Sep 10th, 2018

Healthy Life

UF & MDA Host 2018 Pompe Disease Patient Meeting

Published: Jul 30th, 2018

Lab

Developing Personalized CRISPR-Cas9 Genome Editing Therapy for Pompe Disease

Published: Jul 18th, 2018

Amicus

Amicus Announces Regulatory/Clinical Updates for AT-GAA in Pompe

Published: Jul 6th, 2018

Gene

Gene therapy for pulmonary dysfunction in Pompe

Published: Feb 19th, 2018

Valerion Initiates VAL-1221 Dosing in Patients with Pompe

Published: Jul 11th, 2017

The backstory behind the Pompe patient Trump highlighted to Congress

Published: Mar 2nd, 2017

The 2017 Rare Disease Day video!

Published: Jan 30th, 2017

Lab

UF researchers use gene therapy to treat pulmonary dysfunction in Pompe

Published: Sep 15th, 2016

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