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Audentes Announces Positive Interim Data from First Dose Cohort of ASPIRO
January 4, 2018
A US drugmaker offers to cure rare blindness for $850,000
January 3, 2018
FDA approves first gene therapy for an inherited disease
December 19, 2017
Solid Biosciences Initiates Clinical Trial for Gene Transfer in DMD
December 8, 2017
Solid Biosciences Initiates Clinical Trial for Gene Transfer
November 30, 2017
FDA advisers endorse gene therapy for blindness
October 13, 2017
Join the UCLA Genetic Modifier Study
October 1, 2017
Unique gene therapy prevents, reverses multiple sclerosis in animal model
September 21, 2017
Audentes Therapeutics Announces Dosing of First Patient in ASPIRO
September 21, 2017
Robert Weiner’s huge impact on the muscular dystrophy community
September 15, 2017
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