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Powell Center for Rare Disease Research and Therapy Department of Pediatrics in the College of Medicine
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  1. All Posts
  2. Neuromuscular Diseases
Posted in

Neuromuscular Diseases

Provention Bio Announces Key Findings from Pre-clinical Proof-of-concept Study

January 28, 2021

Prevention Bio

Denison Magazine: The Idea Guy

November 2, 2020

Barry Byrne

Researchers report experimental drug may prolong survival in ALS patients

October 22, 2020

UF

What is holding back gene therapy?

June 30, 2020

lab tubes

Solid Biosciences Presents Data at ASGCT 23rd Annual Meeting

May 14, 2020

Lab

5 Things To Know About Coronavirus And People With Disabilities

April 9, 2020

Coronavirus

The Coronavirus Conundrum: ACE2 and Hypertension Edition

March 23, 2020

Pills

COVID-19 & Duchenne: What you need to know

March 23, 2020

COVID

Coronavirus and Duchenne & Becker muscular dystrophy

March 17, 2020

Coronavirus

Expanded Access Program Launched for Viltolarsen

March 12, 2020

Duchenne

Recent News

  • Zolgensma-Evrysdi Combo Likely Beneficial for SMA Type 1 August 6, 2021
  • PepGen raises $113M to challenge Sarepta in DMD August 5, 2021
  • Sarepta Acquires Investigational Gene Therapy for LGMD2A August 4, 2021
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Powell Center for Rare Disease Research and Therapy Department of Pediatrics in the College of Medicine

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  • Pediatrics Department
  • Powell Gene Therapy Center
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Clinical and Translational Research Building
2004 Mowry Road, Gainesville, FL 32610
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