What You Need to Know About Duchenne Muscular Dystrophy Gene Therapy
Gene therapy is poised to revolutionize how Duchenne is treated, but there are still some problems with this approach that need to be solved.
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Leslie Galloway
What Causes Duchenne Muscular Dystrophy?
Different kinds of mutations on the same gene can all lead to a lack of dystrophin, a protein that’s critical for long-term muscle function.
MDA’s Medical Advisory Team to Help Guide Research and Patient Care
The Muscular Dystrophy Association (MDA) has formed a Medical Advisory Team to provide guidance related to research and clinical care in muscular dystrophy, amyotrophic lateral sclerosis (ALS) and other neuromuscular disorders. https://musculardystrophynews.com/2020/04/28/mda-forms-medical-advisory-team-neuromuscular-disease-experts-guide-research-care/…
